• Rare Disease Desert Symposium 2018

Preliminary Agenda

The Rare Disease Desert Symposium will officially kick off at 1pm MST on Monday, February 26th, with registration at Icagen-T in Tucson, AZ. Attendees coming from the east or west coast of the US will be able to travel that morning, as there are several early flight options to both Tucson and Phoenix. Alternatively, attendees can arrive Sunday, February 25th, and spend Monday morning at Icagen-T for a guided site tour.

Please note the following agenda is in Mountain Standard Time (MST).

Day 1: Monday, February 26, 2018

1:00pm Registration
2:00pm Welcome
Chris Mathes, Ph.D., MBA, Chief Commercial Officer, Icagen
2:05pm Opening Remarks
Ken Wertman, Ph.D., SVP and Site Director, Icagen
2:15pm Keynote Address
Prof. James Spudich, Douglass M. and Nola Leishman Professor of Cardiovascular Disease, Dept. of Biochemistry, Stanford University School of Medicine
Session 1
Muscular Dystrophies 1: DMD
Paul August, Ph.D., VP, Biology, Icagen (Chair)
3:00pm Prof. Louis Kunkel
Professor of Pediatrics, Dept. of Genetics, Harvard University
3:30pm Coffee & Networking Break
4:00pm Prof. Eric Hoffman
Chairman, Department of Integrative Systems Biology, George Washington University
4:30pm Prof. Andy Berglund
Department of Biochemistry and Molecular Biology, Center for NeuroGenetics, University of Florida
5:00pm Prof. Rita Perlingeiro
Cardiovascular Division, University of Minnesota; Lillehei Professor in Stem Cell and Regenerative Cardiovascular Medicine, Lillehei Heart Institute
5:30pm Dr. Jane Larkindale
Executive Director, Duchenne Regulatory Science Consortium (D-RSC), Critical Path Institute
5:50pm Closing Remarks
Doug Krafte, Ph.D., Chief Scientific Officer, Icagen
6:00pm Dinner Reception
Hilton Tucson El Conquistador

Day 2: Tuesday, February 27, 2018

8:00am Continental Breakfast & Registration
8:20am Opening Remarks
Emily Kamer-Golinkoff, Co-Founder of Emily's Entourage
8:30am Keynote Address
Dr. Richard Gregory, Chief Scientific Officer, ImmunoGen
Session 2
Muscular Dystrophies 2: FSHD & EDMD
Prof. Michael Kyba (Chair)
9:15am Dr. Angela Cacace
Vice President, Biology, Fulcrum Therapeutics
9:45am Prof. Michael Kyba
Lillehei Endowed Scholar, Carrie Ramey / CCRF Endowed Professor in Pediatric Cancer Research, Department of Pediatrics
10:15am Prof. Sue Shackleton
Dept. of Molecular and Cell Biology, University of Leicester
10:45am Coffee & Networking Break
Session 3
Other Rare Diseases
(Chair TBA)
11:00am Speaker TBD
11:30am Dr. Christopher VanDeusen
President and co-Founder, Omdana Therapeutics
12:00pm Lunch Break & Posters
Session 4
ALS
Prof. Justin Ichida (Chair)
1:30pm Prof. Justin Ichida
Stem Cell & Regenerative Medicine, Keck School of Medicine, University of Southern California
2:00pm Prof. Aaron Gitler
Genetics, Stanford University
2:30pm Prof. Don Cleveland
Chair, Department of Cellular and Molecular Medicine; Distinguished Professor of Cellular and Molecular Medicine, Medicine, and Neurosciences Member, Ludwig Institute for Cancer Research
3:00pm Coffee Break
Session 5
Cystic Fibrosis
Martin Mense, Ph.D. (Chair)
3:30pm Prof. Robert Bridges
Physiology and Biophysics, Chicago Medical School
4:00pm Dr. Martin Mense
Vice President for Drug Discovery, Cystic Fibrosis Foundation Therapeutics
4:30pm Dr. Sandi Engle
Vertex
5:00pm TBD
5:30pm Close of Symposium and Closing Remarks
Richie Cunningham, CEO, Icagen
6:00pm Reception on deck at Icagen-T for those remaining
Rare Disease Desert Symposium 2018

RARE DISEASE DESERT SYMPOSIUM
FEBRUARY 26-27, 2018

Icagen-T Inc.
2090 E. Innovation Park Drive
Tucson, AZ 85755
+1 520-544-6800

QUESTIONS? PLEASE CONTACT:
Chris Mathes, Ph.D., M.B.A.
Chief Commercial Officer
cmathes@icagen.com

SYMPOSIUM
FOUNDATION PARTNER

Muscular Dystrophy Association

Muscular Dystrophy Association
www.mda.org

SYMPOSIUM
FOUNDATION PARTNER

ALS Arizona Chapter

ALS Association Arizona Chapter
www.alsaz.org

SYMPOSIUM
FOUNDATION PARTNER

FSH Society

FSH Society
www.fshsociety.org

SYMPOSIUM
FOUNDATION PARTNER

Emily's Entourage

Emily's Entourage
www.emilysentourage.org